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While the paper has merits, it falls short of fully supporting its major conclusions. A major technical concern is about the time course of transgene expression and assessment of therapeutic benefits. Day 14 post injection would seem to be too short for onset of gene expression from AAV2, as indicated by the low level of IFN. My doubt is further magnified having reviewed Fig. 2B. This does not appear to be AAV mediated expression of GFP, but background instead.

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[ Last edited by ÌïÔ°1983 on 2011-2-27 at 21:13 ]
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